The UMD-THAP1 mutations database
Record ID: 223

Mutation description


Variation name (cDNA level)Variation name (protein level)Variation statusVariation class
c.173T>Cp.Phe58SerHeterozygousMutation

wt codonwt aamutant codonmutant aamutational eventmutation type
TTTPheTCTSerT->CTs

StructureKey Residue (HCD)Pyrimidin doubletCpG
THAP dom. DNA binding -Yes, coding strandNo

Mutation impact


At the mRNA levelOn restriction map
NANew restriction site(s): none
Lost restriction site(s): none

Conservation (0-1)SIFT (0-1)UMD-predictor (0-100)
0.790.00 (pathogenous)100 (Pathogenous)

Patient and sample data


Sample IDPatient IDFamily IDPatient statusGenderTransmissionGeographic origin
JAP01TOK F0004 I00014ProbandFemaleNo family historyJAPAN

Phenotypic groupDisease
NAGeneralized dystonia

Clinical data


SymptomSeverityAge
Age at last examination
Age of onset8
Handbilateral8
Incomplete clinical description

Reference


Reference IDPubMed IDReference
3824227593
Miyamoto R, Koizumi H, Morino H, Kawarai T, Maruyama H, Mukai Y, Miyashiro A, Sako W, Izumi Y, Kawakami H, Kaji R. DYT6 in Japan-genetic screening and clinical characteristics of the patients. Mov Disord. 2014 Feb;29(2):278-80.