The UMD-THAP1 mutations database
Record ID: 171

Mutation description


Variation name (cDNA level)Variation name (protein level)Variation statusVariation class
c.476T>Ap.Leu159HisHeterozygousMutation

wt codonwt aamutant codonmutant aamutational eventmutation type
CTCLeuCACHisT->ATv

StructureKey Residue (HCD)Pyrimidin doubletCpG
NLS THAP1 dimerizationYes, coding strandNo

Mutation impact


At the mRNA levelOn restriction map
NANew restriction site(s): none
Lost restriction site(s): Dde I

Conservation (0-1)SIFT (0-1)UMD-predictor (0-100)
0.860.00 (pathogenous)100 (Pathogenous)

Patient and sample data


Sample IDPatient IDFamily IDPatient statusGenderTransmissionGeographic origin
CHI02CHE F0003 I0001ProbandFemaleUnknownCHINA

Phenotypic groupDisease
NASegmental dystonia

Clinical data


SymptomSeverityAge
Age at last examination54
Age of onsetface52
Face54
Larynx54
Tongue54

Reference


Reference IDReference
26Unpublished data