The UMD-FBN1 mutations database
Record ID: 511

Mutation description


Variation name (cDNA level)Variation name (protein level)Variation statusVariation class
c.5344T>Cp.Cys1782ArgHeterozygousMutation

wt codonwt aamutant codonmutant aamutational eventmutation type
TGTCysCGTArgT->CTs

StructureKey Residue (HCD)Pyrimidin doubletCpG
cb EGF-like #25 Disulfide bonds 1770-1782 (C3)NoNo

Mutation impact


At the mRNA levelOn restriction map
NANew restriction site(s): none
Lost restriction site(s): none

Conservation (0-1)SIFT (0-1)UMD-predictor (0-100)
10.00 (pathogenous)100 (Pathogenous)

Patient and sample data


Sample IDPatient statusGenderTransmissionAge of onsetAge of deathGeographic origin
FRA01BOU F0143 I0182ProbandMalefamilialFRANCE

Phenotypic groupDisease
NAClassical MFS

Clinical data


SymptomSeverity
C-Aortic insufficiencymoderate
C-Asc. aortic dissection
C-Desc. aortic dilatation (thor or abdo)
C-Mitral valve prolapse
CNS-Lumbosacral dural ectasia
O-Ectopia lentisbilateral
O-Flat cornea (<42 dp) (m)
O-Increased axial length of globe (m)
O-Myopia
O-Retinal detachment
S-Crowding teeth (m)
S-Dolichostenomelia
S-High arched palate
S-Joint limitations
S-Kyphosis
S-Plain pes planus (M)(1)
S-Protusio acetabulæ (M)(2)
S-Scoliosis > 20° (M)(1)
SI-Significant striae atrophicae (m)(1)

Reference


Reference IDPubMed IDReference
6412938084
Collod-B*roud G, Le Bourdelles S, Ades L, Ala-Kokko L, Booms P, Boxer M, Child A, Comeglio P, De Paepe A, Hyland JC, Holman K, Kaitila I, Loeys B, Matyas G, Nuytinck L, Peltonen L, Rantamaki T, Robinson P, Steinmann B, Junien C, B*roud C, Boileau C. "Update of the UMD-FBN1 mutation database and creation of an FBN1 polymorphism database". Hum Mutat. 2003 Sep;22(3):199-208.