The UMD-FBN1 mutations database
Record ID: 175

Mutation description


Variation name (cDNA level)Variation name (protein level)Variation statusVariation class
c.3546C>Gp.Cys1182TrpHeterozygousMutation

wt codonwt aamutant codonmutant aamutational eventmutation type
TGCCysTGGTrpC->GTv

StructureKey Residue (HCD)Pyrimidin doubletCpG
cb EGF-like #14 Disulfide bonds 1182-1195 (C5)NoNo

Mutation impact


At the mRNA levelOn restriction map
NANew restriction site(s): BstK I, Dsa V, Nla IV, ScrF I
Lost restriction site(s): BstN I, EcoR II

Conservation (0-1)SIFT (0-1)UMD-predictor (0-100)
0.670.00 (pathogenous)100 (Pathogenous)

Patient and sample data


Sample IDPatient statusGenderTransmissionAge of onsetAge of deathGeographic origin
ITA01FLO F0001 I03ProbandMalefamilialbefore 3 monthsITALIA

Phenotypic groupDisease
NAClassical MFS

Clinical data


SymptomSeverity
C-Asc. aortic dilatation
C-Mitral valve prolapse
CF-Blue sclerae
CF-Dolichocephaly
O-Ectopia lentis
O-Myopia >3 diopters (1)severe
S-Arachnodactyly (M)
S-High arched palate
S-Joint hypermobility (m)
S-Pectus excavatum moderate (m)(1)
S-Scoliosis > 20° (M)(1)
SI-Significant striae atrophicae (m)(1)
SI-Tendency to ecchymosis
SI-Translucent skin

Reference


Reference IDPubMed IDReference
509236141
Pepe G, Giusti B, Attanasio M, Comeglio P, Porciani MC, Giurlani L, Montesi GF, Calamai GC, Vaccari M, Favilli S, Abbate R, Gensini GF. "A major involvement of the cardiovascular system in patients affected by Marfan syndrome: novel mutations in fibrillin 1 gene". Mol Cell Cardiol 1997 Jul;29(7):1877-84.